Gene therapy for sickle cell disease durability Gene therapy for sickle cell disease durability. Prueksapraopong C, Kohn DB. Blood Adv. 2026 Aug 25;10(16):5741. doi: 10.1182/bloodadvances.2026021246. PMID: 42335206 PMID: https://pubmed.ncbi.nlm.nih.gov/42335206/ (opens in a new tab)