Prime Editing for p47phox-Deficient Chronic Granulomatous Disease
Prime Editing for p47phox-Deficient Chronic Granulomatous Disease. Gori JL, Haddad E, Frangoul H, Kohn DB, Morris EC, Martin BN, Deary BA, Nickerson M, Scholz RL, Fernandez I, Leveille K, De Ravin SS, Kang EM, Pierzynski M, Estwick T, Littel P, Kuhns DB, Long Priel DA, Teira P, Turvey S, Arnold J, Evans MD, McManus M, Carpenter B, Waterman DP, Anzalone AV, Petrusich A, Osuna CE, O’Malley TT, Stewart-Ornstein J, Heath JM, Nehilla BJ, Asmal M, Malech HL. N Engl J Med. 2026 Mar 26;394(12):1195-1203. doi: 10.1056/NEJMoa2509807. Epub 2025 Dec 7. PMID: 41358590 Free article. Clinical Trial
